Latest News

Nate Plasman is a Duchenne Muscular Dystrophy (DMD) parent advocate, a devoted husband to his wife of 20 years, Sara, and a proud father...

Lauren Holder is a research ambassador, advocate, and committed caregiver. After discovering she was gene-positive for Huntington’s...

On June 17, the Institute for Gene Therapies (IGT), in partnership with the Alliance for Regenerative Medicine (ARM), convened a panel...

Amanda Moore is a devoted mother, advocate, and CEO of the Angelman Syndrome Foundation. After adopting her two sons, Jackson and Baden,...

Lesa Brackbill is a passionate mother, advocate, author, and member of IGT’s Patient Advocacy Advisory Council. After her daughter...

Authors: IGT Chairman Erik Paulsen, Scientific Academic and Medical Council Chair Donna Christian-Christensen, M.D. As our nation’s...