September is Newborn Screening Awareness Month, a dedicated time to educate the public about this critical screening. IGT advocates for...

By Jennifer McNary, mother of two sons with Duchenne muscular dystrophy, patient advocate and founder of One Rare. For all the incredible...

One of our founding Patient Advisory Council Members, the EveryLife Foundation for Rare Diseases, is a 501(c)(3) nonprofit, nonpartisan...

Proposed rule advances longstanding priority for gene therapy stakeholders FOR IMMEDIATE RELEASE July 20, 2020 CONTACT: Macey Kostbar,...

On Monday, July 13, the Institute for Gene Therapies (IGT) held a conversation with recognized experts on the CMS proposed rule that...

On Monday, July 13, 2020 at 4 PM Eastern Time, the Institute for Gene Therapies (IGT) will host a conversation with recognized experts...

FOR IMMEDIATE RELEASE CONTACT: Macey Kostbar msevcik@gene-therapies.org WASHINGTON, DC (June 18, 2020) – Below is a statement from the...

Susan Ruediger is the founder and CEO of the CMT Research Foundation — a nonprofit organization with the single focus to expedite...

Join Axios and IGT on May 4, 2020 at 12:30pm Eastern for a live, virtual event on essential medical research outside the scope of the...

By Jenn McNary, Patient Advocate, Founder of One Rare While most Americans are beginning to talk excitedly – albeit cautiously – about...