Patient Perspective: Cure SMA September is Newborn Screening Awareness Month, a dedicated time to educate the public about this critical screening. IGT advocates for t...
Dr. Peter Marks Clarifies FDA’s Approach to Gene Therapies After CRL for Hemophilia A Treatment By Jennifer McNary, mother of two sons with Duchenne muscular dystrophy, patient advocate and founder of One Rare. For all the incredible...
Patient Perspective: EveryLife Foundation for Rare Diseases One of our founding Patient Advisory Council Members, the EveryLife Foundation for Rare Diseases, is a 501(c)(3) nonprofit, nonpartisan o...
Institute for Gene Therapies Comments on CMS Proposed Rule on Value-based Purchasing Arrangements Proposed rule advances longstanding priority for gene therapy stakeholders FOR IMMEDIATE RELEASE July 20, 2020 CONTACT: Macey Kostbar, ms...
IGT Webinar on CMS Proposed Rule on Value-based Purchasing On Monday, July 13, the Institute for Gene Therapies (IGT) held a conversation with recognized experts on the CMS proposed rule that make...
IGT to Host Webinar on CMS Proposed Rule on Value-based Purchasing On Monday, July 13, 2020 at 4 PM Eastern Time, the Institute for Gene Therapies (IGT) will host a conversation with recognized experts wh...
IGT Statement on CMS Proposed Rule to Facilitate Value-based Purchasing Arrangements FOR IMMEDIATE RELEASE CONTACT: Macey Kostbar msevcik@gene-therapies.org WASHINGTON, DC (June 18, 2020) – Below is a statement from the I...
Patient Perspective: Susan Ruediger Susan Ruediger is the founder and CEO of the CMT Research Foundation — a nonprofit organization with the single focus to expedite treatme...
IGT Joins Axios to Host Webinar on Medical Research During a Crisis Join Axios and IGT on May 4, 2020 at 12:30pm Eastern for a live, virtual event on essential medical research outside the scope of the imm...
FDA’s Dr. Peter Marks on Ways to Preserve Ongoing Medical Research During the Pandemic By Jenn McNary, Patient Advocate, Founder of One Rare While most Americans are beginning to talk excitedly – albeit cautiously – about ge...
